Case study

Best-in-Class LRRK2 Therapies for Parkinson’s Disease

Challenge

Following Alzheimer’s disease, Parkinson’s disease is the second most common neurodegenerative disorder in the US. LRRK2 is one of the most promising drug targets for Parkinson’s disease. There are currently some drug candidates in clinical trials, but no FDA-approved drug. The goal: to pioneer the first approved therapy in this large and critical market.

Solution & Impact

BIOPTIC AI quickly identified a chemically novel 0.86 uM LRRK2 inhibitor from a vast chemical space of 39B molecules. This discovery brings us closer to delivering a best-in-class solution for an underserved patient population.

Chemical spase

39B

Search time

4H

Tested

87 compounds

Total cost

$17K

Novelty (Tanimoto ECFP4)

max 0.4

Hit rate (<10 μM)

4.6%

Best hit

0.86 μM

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